Key lessons from the first international treatment eligibility committee: the case of metachromatic leukodystrophy

Schoenmakers, Daphne H.; Asbreuk, Marije A. B. C.; Martin, Tamara; Datema, Mareen; Beerepoot, Shanice; Inbar-Feigenberg, Michal; Groescheli, Samuel; Kehreri, Christiane; Obergj, Andreas; Sevin, Caroline; Fumagalli, Francesca; Bergner, Caroline G.; Vieirap, Paivi; Bley, Annette; Uusimaap, Johanna; Horns, Morten Andreas; Brozova, Klara; Stogmann, Eva; Pichlerw, Herbert; Luftinger, Roswitha; Eklund, Erik A.; Mochel, Fanny; Adang, Laura A.; Laugwitz, Lucia; Boelens, Jaap Jan; Calbi, Valeria; Darling, Alejandra; Garcia-Cazorla, Angeles; Gronborg, Sabine W.; Lindemans, Caroline A.; Hasselt, Peter M. van; Hollak, Carla E. M.; de Koning, Tom J.; Ram, Dipak; Dekker, Hanka; Schols, Ludger; Zerem, Ayelet; Graessner, Holm; Wolf, Nicole I.

dc.contributor.author	Martin, Tamara
dc.contributor.author	Laugwitz, Lucia
dc.contributor.author	Graessner, Holm
dc.contributor.author	Gröschel, Samuel
dc.contributor.author	Kehrer, Christiane
dc.contributor.author	Schöls, Ludger
dc.date.accessioned	2025-09-03T12:38:12Z
dc.date.available	2025-09-03T12:38:12Z
dc.date.issued	2025
dc.identifier.issn	1090-3798
dc.identifier.uri	http://hdl.handle.net/10900/169903
dc.language.iso	en	de_DE
dc.publisher	London : Elsevier Sci Ltd	de_DE
dc.relation.uri	http://dx.doi.org/10.1016/j.ejpn.2025.05.012	de_DE
dc.subject.ddc	610	de_DE
dc.title	Key lessons from the first international treatment eligibility committee: the case of metachromatic leukodystrophy	de_DE
dc.type	Article	de_DE
utue.quellen.id	20250630000000_00102
utue.publikation.seiten	72-81	de_DE
utue.personen.roh	Schoenmakers, Daphne H.
utue.personen.roh	Asbreuk, Marije A. B. C.
utue.personen.roh	Martin, Tamara
utue.personen.roh	Datema, Mareen
utue.personen.roh	Beerepoot, Shanice
utue.personen.roh	Inbar-Feigenberg, Michal
utue.personen.roh	Groescheli, Samuel
utue.personen.roh	Kehreri, Christiane
utue.personen.roh	Obergj, Andreas
utue.personen.roh	Sevin, Caroline
utue.personen.roh	Fumagalli, Francesca
utue.personen.roh	Bergner, Caroline G.
utue.personen.roh	Vieirap, Paivi
utue.personen.roh	Bley, Annette
utue.personen.roh	Uusimaap, Johanna
utue.personen.roh	Horns, Morten Andreas
utue.personen.roh	Brozova, Klara
utue.personen.roh	Stogmann, Eva
utue.personen.roh	Pichlerw, Herbert
utue.personen.roh	Luftinger, Roswitha
utue.personen.roh	Eklund, Erik A.
utue.personen.roh	Mochel, Fanny
utue.personen.roh	Adang, Laura A.
utue.personen.roh	Laugwitz, Lucia
utue.personen.roh	Boelens, Jaap Jan
utue.personen.roh	Calbi, Valeria
utue.personen.roh	Darling, Alejandra
utue.personen.roh	Garcia-Cazorla, Angeles
utue.personen.roh	Gronborg, Sabine W.
utue.personen.roh	Lindemans, Caroline A.
utue.personen.roh	Hasselt, Peter M. van
utue.personen.roh	Hollak, Carla E. M.
utue.personen.roh	de Koning, Tom J.
utue.personen.roh	Ram, Dipak
utue.personen.roh	Dekker, Hanka
utue.personen.roh	Schols, Ludger
utue.personen.roh	Zerem, Ayelet
utue.personen.roh	Graessner, Holm
utue.personen.roh	Wolf, Nicole I.
dcterms.isPartOf.ZSTitelID	European Journal of Paediatric Neurology	de_DE
dcterms.isPartOf.ZS-Volume	57	de_DE
utue.fakultaet	04 Medizinische Fakultät	de_DE