Development of Methodology and Study Protocol : Safety and Efficacy of a Single Subretinal Injection of rAAV.hCNGA3 in Patients with CNGA3-Linked Achromatopsia Investigated in an Exploratory Dose-Escalation Trial

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Development of Methodology and Study Protocol : Safety and Efficacy of a Single Subretinal Injection of rAAV.hCNGA3 in Patients with CNGA3-Linked Achromatopsia Investigated in an Exploratory Dose-Escalation Trial

Author: Kahle, Nadine A.; Peters, Tobias; Zobor, Ditta; Kuehlewein, Laura; Kohl, Susanne; Zhour, Ahmad; Werner, Annette; Seitz, Immanuel P.; Sothilingam, Vithiyanjali; Michalakis, Stylianos; Biel, Martin; Ueffing, Marius; Zrenner, Eberhart; Bartz-Schmidt, Karl U.; Fischer, M. Dominik; Wilhelm, Barbara J. C.
Tübinger Autor(en):
Peters, Tobias
Zobor, Ditta
Kohl, Susanne
Zhour, Ahmad
Werner, Annette
Sothilingam, Vithiyanjali
Ueffing, Marius
Zrenner, Eberhart
Kahle, Nadine
Kühlewein, Laura
Seitz, Immanuel Philipp
Bartz-Schmidt, Karl Ulrich
Fischer, Manuel Dominik
Wilhelm, Barbara
Published in: Human Gene Therapy Clinical Development (2018), Bd. 29, H. 3, S. 121-131
Verlagsangabe: Mary Ann Liebert
Language: English
Full text: http://dx.doi.org/10.1089/humc.2018.088
ISSN: 2324-8645
DDC Classifikation: 570 - Life sciences; biology
610 - Medicine and health
Dokumentart: Artikel
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