Methodological challenges in monitoring new treatments for rare diseases: lessons from the cryopyrin-associated periodic syndrome registry

Tilson, Hugh; Primatesta, Paola; Kim, Dennis; Rauer, Barbara; Hawkins, Philip N.; Hoffman, Hal M.; Kuemmerle-Deschner, Jasmin; van der Poll, Tom; Walker, Ulrich A.

dc.contributor.author	Kümmerle-Deschner, Jasmin
dc.date.accessioned	2014-02-18T06:47:52Z
dc.date.available	2014-02-18T06:47:52Z
dc.date.issued	2013
dc.identifier.issn	1750-1172
dc.identifier.uri	http://hdl.handle.net/10900/41791
dc.language.iso	en	en
dc.publisher	Biomed Central Ltd	de_DE
dc.relation.uri	http://dx.doi.org/10.1186/1750-1172-8-139	de_DE
dc.rights	info:eu-repo/semantics/closedAccess
dc.subject.ddc	610	de_DE
dc.title	Methodological challenges in monitoring new treatments for rare diseases: lessons from the cryopyrin-associated periodic syndrome registry	de_DE
dc.type	Article	de_DE
utue.quellen.id	20140116051827_00786	de_DE
utue.personen.roh	Tilson, Hugh
utue.personen.roh	Primatesta, Paola
utue.personen.roh	Kim, Dennis
utue.personen.roh	Rauer, Barbara
utue.personen.roh	Hawkins, Philip N.
utue.personen.roh	Hoffman, Hal M.
utue.personen.roh	Kuemmerle-Deschner, Jasmin
utue.personen.roh	van der Poll, Tom
utue.personen.roh	Walker, Ulrich A.
dcterms.isPartOf.ZSTitelID	Orphanet Journal of Rare Diseases	de_DE
dcterms.isPartOf.ZS-Issue	Article 139	de_DE
dcterms.isPartOf.ZS-Volume	8	de_DE
utue.fakultaet	04 Medizinische Fakultät	de_DE