Short-Term Outcomes of Pediatric Patients With Mild Autosomal Recessive RPE65-Associated Retinal Dystrophy Treated With Voretigene Neparvovec

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dc.contributor.author Merle, David A.
dc.contributor.author Dimopoulos, Spyridon
dc.contributor.author Kohl, Susanne
dc.contributor.author Mazzola, Pascale
dc.contributor.author Haack, Tobias
dc.contributor.author Wolfram, Lasse
dc.contributor.author Kempf, Melanie
dc.contributor.author Stingl, Krunoslav
dc.contributor.author Stingl, Katarina
dc.contributor.author Kühlewein, Laura
dc.date.accessioned 2026-10-27T09:25:55Z
dc.date.available 2026-10-27T09:25:55Z
dc.date.issued 2025
dc.identifier.issn 2164-2591
dc.identifier.uri http://hdl.handle.net/10900/185013
dc.language.iso en de_DE
dc.publisher Rockville : Assoc Research Vision Ophthalmology Inc de_DE
dc.relation.uri http://dx.doi.org/10.1167/tvst.14.8.8 de_DE
dc.subject.ddc 610 de_DE
dc.title Short-Term Outcomes of Pediatric Patients With Mild Autosomal Recessive RPE65-Associated Retinal Dystrophy Treated With Voretigene Neparvovec de_DE
dc.type Article de_DE
utue.quellen.id 20251118000000_01248
utue.personen.roh Merle, David A.
utue.personen.roh Hertens, Leen
utue.personen.roh Dimopoulos, Spyridon
utue.personen.roh Kohl, Susanne
utue.personen.roh Van Haute, Manon
utue.personen.roh De Baere, Elfride
utue.personen.roh De Bruyne, Marieke
utue.personen.roh Janssens, Barbara
utue.personen.roh Ruther, Klaus
utue.personen.roh Huchzermeyer, Cord
utue.personen.roh Mazzola, Pascale
utue.personen.roh Nerinckx, Fanny
utue.personen.roh Haack, Tobias
utue.personen.roh Wolfram, Lasse
utue.personen.roh Kempf, Melanie
utue.personen.roh Kuhlewein, Laura
utue.personen.roh Stingl, Krunoslav
utue.personen.roh Leroy, Bart P.
utue.personen.roh Stingl, Katarina
dcterms.isPartOf.ZSTitelID Translational Vision Science & Technology de_DE
dcterms.isPartOf.ZS-Issue Article 8 de_DE
dcterms.isPartOf.ZS-Volume 14 (8) de_DE
utue.fakultaet 04 Medizinische Fakultät de_DE


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