Core protocol development for phase 2/3 clinical trials in the leukodystrophy vanishing white matter: a consensus statement by the VWM consortium and patient advocates

Schoenmakers, Daphne H.; Leferink, Prisca S.; Vanderver, Adeline; Bonkowsky, Joshua L.; Kraegeloh-Mann, Ingeborg; Bernard, Genevieve; Bertini, Enrico; Fatemi, Ali; Fogel, Brent L.; Wolf, Nicole I.; Skwirut, Donna; Buck, Allyson; Holberg, Brett; Saunier-Vivar, Elise F.; Rauner, Robert; Dekker, Hanka; van Bokhoven, Pieter; Stellingwerff, Menno D.; Berkhof, Johannes; van der Knaap, Marjo S.

Core protocol development for phase 2/3 clinical trials in the leukodystrophy vanishing white matter: a consensus statement by the VWM consortium and patient advocates

Autor(en):

Schoenmakers, Daphne H.; Leferink, Prisca S.; Vanderver, Adeline; Bonkowsky, Joshua L.; Kraegeloh-Mann, Ingeborg; Bernard, Genevieve; Bertini, Enrico; Fatemi, Ali; Fogel, Brent L.; Wolf, Nicole I.; Skwirut, Donna; Buck, Allyson; Holberg, Brett; Saunier-Vivar, Elise F.; Rauner, Robert; Dekker, Hanka; van Bokhoven, Pieter; Stellingwerff, Menno D.; Berkhof, Johannes; van der Knaap, Marjo S.

Tübinger Autor(en):

Krägeloh-Mann, Ingeborg

Erschienen in:

Bmc Neurology (2023), Bd. 23, H. 1

Verlagsangabe:

London : Bmc

Sprache:

Englisch

Referenz zum Volltext:

http://dx.doi.org/10.1186/s12883-023-03354-9

ISSN:

1471-2377