Preparing n-of-1 Antisense Oligonucleotide Treatments for Rare Neurological Diseases in Europe: Genetic, Regulatory, and Ethical Perspectives

Synofzik, Matthis; Van Roon-Mom, Willeke M. C.; Marckmann, Georg; van Duyvenvoorde, Hermine A.; Graessner, Holm; Schule, Rebecca; Aartsma-Rus, Annemieke

dc.contributor.author	Synofzik, Matthis
dc.contributor.author	Graessner, Holm
dc.contributor.author	Schüle, Rebecca
dc.date.accessioned	2023-04-27T09:13:21Z
dc.date.available	2023-04-27T09:13:21Z
dc.date.issued	2022
dc.identifier.issn	2159-3337
dc.identifier.uri	http://hdl.handle.net/10900/139762
dc.language.iso	en	de_DE
dc.publisher	Mary Ann Liebert, Inc	de_DE
dc.relation.uri	http://dx.doi.org/10.1089/nat.2021.0039	de_DE
dc.subject.ddc	540	de_DE
dc.subject.ddc	570	de_DE
dc.subject.ddc	610	de_DE
dc.title	Preparing n-of-1 Antisense Oligonucleotide Treatments for Rare Neurological Diseases in Europe: Genetic, Regulatory, and Ethical Perspectives	de_DE
dc.type	Article	de_DE
utue.quellen.id	20220728000000_02989
utue.publikation.seiten	83-94	de_DE
utue.personen.roh	Synofzik, Matthis
utue.personen.roh	Van Roon-Mom, Willeke M. C.
utue.personen.roh	Marckmann, Georg
utue.personen.roh	van Duyvenvoorde, Hermine A.
utue.personen.roh	Graessner, Holm
utue.personen.roh	Schule, Rebecca
utue.personen.roh	Aartsma-Rus, Annemieke
dcterms.isPartOf.ZSTitelID	Nucleic Acid Therapeutics	de_DE
dcterms.isPartOf.ZS-Issue	2	de_DE
dcterms.isPartOf.ZS-Volume	32	de_DE
utue.fakultaet	04 Medizinische Fakultät	de_DE