Allele-specific targeting of mutant ataxin-3 by antisense oligonucleotides in SCA3-iPSC-derived neurons

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Allele-specific targeting of mutant ataxin-3 by antisense oligonucleotides in SCA3-iPSC-derived neurons

Author: Hauser, Stefan; Helm, Jacob; Kraft, Melanie; Korneck, Milena; Huebener-Schmid, Jeannette; Schoels, Ludger
Tübinger Autor(en):
Hauser, Stefan
Helm, Jacob
Kraft, Melanie
Korneck, Milena
Hübener-Schmid, Jeannette
Schöls, Ludger
Published in: Molecular Therapy - Nucleic Acids (2022), Bd. 27, S. 99-108
Verlagsangabe: Cell Press
Language: English
Full text: http://dx.doi.org/10.1016/j.omtn.2021.11.015
ISSN: 2162-2531
DDC Classifikation: 610 - Medicine and health
Dokumentart: Article
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